Scientists have created a new gene editing tool that tweaks the individual RNA ‘letters’ in human cells without making changes to the entire genome, paving the way for therapies that can reverse disease-causing mutations.
The molecular system, called RNA Editing for Programmable A to I Replacement(REPAIR) has profound potential as a tool for both research and disease treatment. REPAIR is based on the gene editing tool CRISPR that can be used to modify DNA in cells.
